A novel variant c.7104 + 6T > A of ABCA12 linked to autosomal recessive congenital ichthyosis verified by minigene splicing assay
2024

New Genetic Variant Linked to Skin Disorder

Sample size: 1 publication Evidence: moderate

Author Information

Author(s): Zhu Linyan, Zhou Rui, Zhang Lianxiao, Chen Mei, Zhang Shengmin, Huang Xiaxi, Shi Yubo, Ding Huiqing

Primary Institution: The First Affiliated Hospital of Ningbo University

Hypothesis

Can a novel variant in the ABCA12 gene cause autosomal recessive congenital ichthyosis?

Conclusion

The study identified a new genetic variant in the ABCA12 gene that causes congenital ichthyosis in a fetus.

Supporting Evidence

  • A compound heterozygous variation in the ABCA12 gene was identified in the fetus.
  • The novel variant was classified as a Variant of Uncertain Significance (VUS).
  • Minigene assays confirmed that the variant affects splicing, leading to abnormal mRNA.

Takeaway

Scientists found a new change in a gene that can cause a skin problem in babies, helping us understand this condition better.

Methodology

Whole-exome sequencing and Sanger sequencing were used to identify gene variants, and a minigene assay was performed to evaluate the functional effects of the variant.

Limitations

The study is based on a single case, limiting the generalizability of the findings.

Participant Demographics

A 24-year-old healthy woman and her fetus.

Digital Object Identifier (DOI)

10.3389/fped.2024.1505924

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